News Lipid nanoparticle mRNA therapy improves survival in mouse models of maple syrup urine diseaseAugust 27, 2024 A hairpin loop from a pre-mRNA. Highlighted are the nucleobases (green) and the ribose-phosphate backbone…
News Lung-targeting lipid nanoparticles with CRISPR components successfully treat cystic fibrosis mouse modelsJune 27, 2024 A team of medical researchers from the University of Texas Southwestern Medical Center, Case Western…